Decisions / 5775
final resolution2022-12-15active

Arzneimittel-Richtlinie/Anlage XII: Cerliponase alfa - Neubewertung nach Fristablauf (Neuronale Ceroid-Lipofuszinose Typ 2)

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G-BA source · retrieved 2026-08-05

Structured conclusion

Final result by patient group

1 source-verified result

Patient group

Patientinnen und Patienten mit neuronaler Ceroid-Lipofuszinose (NCL) Typ 2, auch als Tripeptidyl-Peptidase 1 (TPP1)-Mangel bezeichnet

Hint of major added benefit

Comparator

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Decision orientation

What the G-BA did

4 cited claims

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Official metadata

Decision date
2022-12-15
Effective
15.12.2022
Action type
final resolution
Committee
Arzneimittel

Case context

Listed normative targets

directiveArzneimittel-Richtlinie
directive annexAnlage XII: Nutzenbewertung nach § 35a SGB V

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Official document package