Decisions / 6961
final resolution2024-12-19active

Arzneimittel-Richtlinie/Anlage XII: Tofersen (Amyotrophe Lateralsklerose (ALS))

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G-BA source · retrieved 2026-08-05

Structured conclusion

Final result by patient group

1 source-verified result

Patient group

Erwachsene mit amyotropher Lateralsklerose (ALS), die mit einer Mutation im Superoxid- Dismutase 1 (SOD1)-Gen assoziiert ist

Hint of non quantifiable added benefit

Comparator

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Decision orientation

What the G-BA did

4 cited claims

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Official metadata

Decision date
2024-12-19
Effective
19.12.2024
Action type
final resolution
Committee
Arzneimittel

Case context

Listed normative targets

directiveArzneimittel-Richtlinie
directive annexAnlage XII: Nutzenbewertung nach § 35a SGB V

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Official document package